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Supporting those affected by Niemann-Pick diseases

NPUK 23rd Annual Family Conference

The NPUK 23rd Annual Family Conference took place 16-18th September 2016 at Wyboston Lakes

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Latest news

03.08.16

CTD Holdings Receives FDA Fast Track Designation for Development of Trappsol® Cyclo™ to Treat Niemann-Pick Disease Type C

The U.S. Food and Drug Administration (FDA) has granted Fast Track designation to Trappsol® Cyclo™ for the treatment of systemic Niemann-Pick Disease Type C (NPC), a rare and fatal genetic disease. Trappsol® Cyclo™ is the Company's proprietary formulation of hydroxypropyl beta cyclodextrin in development for the treatment of NPC; it has previously been designated an Orphan Drug by the FDA and the European Medicines Agency.

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03.08.16

Jim Green: Stepping Down as NPUK Trustee

Jim Green, a founding member of NPUK all the way back in 1991 - and therefore an individual who has been connected to Niemann-Pick UK for over 25 years, is stepping down from the charity's Board of Trustees. ..

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