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Niemann-Pick Disease

Niemann-Pick diseases are a group of rare inherited lysosomal storage disorders that can affect both children and adults.

Acid Sphingomyelinase Deficiency (ASMD) includes Niemann-Pick Disease Type A (NP-A) and Type B (NP-B), which are caused by a lack of the enzyme acid sphingomyelinase leading to a build-up of toxic materials in the body.

Niemann-Pick Disease Type C (NP-C) is a devastating neurodegenerative disease caused by an accumulation of lipids (fats) in the liver, brain and spleen.

Niemann-Pick Disease

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25.08.16

CTD Holdings to Host Webinar to Provide Update on Trappsol® Cyclo™ Drug Development Program for Treatment of Niemann-Pick Disease Type C

CTD Holdings, Inc. (OTCQB: CTDH), a clinical stage biotechnology company that develops cyclodextrin-based products for the treatment of disease, today announced that it will host a webinar to provide details of the Company’s recently initiated Phase I clinical trial in the U.S. and Phase I/II clinical trial in the EU, both evaluating CTD’s proprietary formulation of hydroxypropyl beta cyclodextrin, Trappsol® Cyclo™, for the treatment of Niemann-Pick Disease Type C (NPC). NPC is a rare and fatal genetic disease that damages the brain, lung, liver, spleen, and other organs.

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25.08.16

NPUK Annual Family Conference & Interactive Workshop 2017

We are looking forward to our next Annual Family Conference & Interactive Workshop, and we hope you are too! The event is the biggest in the NPUK calendar, and this year will be held 22nd-24th September 2017 at the Mercure Haydock Hotel, Merseyside, UK.

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