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Posts filed in: "Uncategorized"

  1. 11.12.18

    Orphazyme expects to announce results of full data set for Niemann-Pick disease Type C (NPC) Phase II/III trial in Q1 2019

    Orphazyme expects to announce results of full data set for Niemann-Pick disease Type C (NPC) Phase II/III trial in Q1 2019...

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  2. 30.11.18

    Mallinckrodt Responds to Global Community Questions on VTS-270 Trial

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  3. 16.11.18

    NPUK News: Autumn 2018

    We are happy to announce that the latest issue of NPUK News (Autumn 2018) is now available. This time around it is a bumper edition featuring everything from the Annual Family Conference to BBC Children in Need, with guest articles from Shona Beveridge, Jenny Charman, and Dave Smith...and so much more!

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  4. 07.11.18

    Mallinckrodt: VTS-270 Phase 2b.3 Data Announcement

    The following letter from Mallinckrodt's Sheila Talafous, Director, Advocacy Relations and Derek Naten, Senior Director, Government Relations & Advocacy refers to the VTS-270 Phase 2b.3, as well as expanded access and compassionate use programs.

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  5. 04.10.18

    CTD announces encouraging top-line data from two ongoing clinical trials of Trappsol® Cyclo™ administered intravenously in Niemann Pick Disease Type C (NPC)

    CTD announces encouraging top-line data from two ongoing clinical trials of Trappsol® Cyclo™ administered intravenously in Niemann Pick Disease Type C (NPC)

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