NPUK relies entirely on voluntary donations and fundraising to enable us to continue our work in supporting the children, adults, and families that are affected by Niemann-Pick disease. We’ve only been able to achieve what we have thanks to the voluntary donations and fundraising efforts of people like you. However, we know we can achieve much more so please continue to support us in any way you can – your kindness will help change lives.
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Thank you from everyone here are NPUK!
In the days and weeks to come, Orphazyme will continue to communicate openly with patient organizations and clinical trial investigators around the globe to share the latest information regarding our efforts as the situation develops. Meanwhile please utilize attached FAQs to answer questions if any about our trials...Read more
OXFORD, UK / ACCESSWIRE / March 25, 2020 / IntraBio Inc., a late-stage biopharmaceutical company, today announced that the US Food and Drug Administration (FDA) has granted Fast Track designation to its lead compound (IB1001) for the treatment of Niemann-Pick disease Type C (NPC)...Read more