NPUK relies entirely on voluntary donations and fundraising to enable us to continue our work in supporting the children, adults, and families that are affected by Niemann-Pick disease. We’ve only been able to achieve what we have thanks to the voluntary donations and fundraising efforts of people like you. However, we know we can achieve much more so please continue to support us in any way you can – your kindness will help change lives.
Your donations, whether big or small, make a difference:
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Thank you from everyone here are NPUK!
We are pleased to share the latest update from Orphazyme entitled 'Orphazyme reports positive results from full data set of Phase II/III arimoclomol trial in Niemann-Pick disease Type C (NPC)'.Read more
CTD Holdings: Annual conference offers opportunities for academic researchers and industry representatives to exchange information on novel therapeutic interventions...Read more