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Mallinckrodt Pharmaceuticals Statement: Adrabetadex for NPC-1

Posted: 16.07.20

“Please take a moment to read this important announcement from Mallinckrodt Pharmaceuticals in regard to the clinical trial of Adrabetadex for NPC-1. We recognise that this may be a surprising and disappointing development for our community as a whole.  Please be assured that we are advocating for further, clearer information and will follow up with our response and next steps shortly.”

Sandra Cowie, President, INPDA

Joslyn Crowe, Executive Director, NNPDF

Toni Mathieson, Chief Executive, NPUK

Advocacy email 7.15.20FINAL


Dr. Elizabeth Berry-Kravis and MNK are hosting a webinar on Thursday, July 16 at 8 PM EST to answer questions from the NPC community.

Link as as follows (password:050409):