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  1. 02.07.21

    NPUK are hiring! (Fundraising Officer)

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  2. 30.06.21

    Orphazyme presents 36-month data supporting durable response to arimoclomol during Parseghian Scientific Conference for NPC Research

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  3. 18.06.21

    Orphazyme: NPC Community Notification

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  4. 11.05.21

    Cyclo Therapeutics Appoints Lori McKenna Gorski as Global Head of Patient Advocacy

    GAINESVILLE, FL–(Businesswire)–May 11, 2021–Cyclo Therapeutics, Inc. (Nasdaq: CYTH) (“Cyclo Therapeutics” or the “Company”), a clinical stage biotechnology company dedicated to developing life-changing medicines through science and innovation for patients and families suffering from diseases, announced today it has appointed Lori McKenna Gorski as Global Head of Patient Advocacy...

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  5. 06.05.21

    ARDEnt publishes its findings on how the fragile rare disease ecosystem was disproportionately impacted by the COVID-19 pandemic

    Today Action for Rare Disease Empowerment (ARDEnt) has published its findings andrecommendations in the report ‘Making The Unseen Seen: Rare disease and lessons learned from the COVID-19 pandemic’...

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