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  1. 05.01.21

    Cyclo Therapeutics Announces Positive Efficacy Data from Extension Protocol with Trappsol® Cyclo™ in Patients with Niemann-Pick Disease Type C

    Home-based intravenous infusions of Trappsol® Cyclo™ for up to one year show improvement in disease features or disease stabilization...

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  2. 05.01.21

    NPUK 2020 Support Fund

    In recognition that many in our community are being impacted by the events of 2020, Trustees of NPUK and The Hollie Foundation, in recognition of their shared goals, have designated funds to create a new grant scheme for patients and families. The aim of this fund is to assist those experiencing hardship or unexpected expense, which threatens to impact their physical or mental well-being...

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  3. 28.12.20

    Orphazyme Provides Regulatory Update on Arimoclomol for NPC

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  4. 21.12.20

    Latest information for clinically extremely vulnerable adults and children

    Both the British Inherited Metabolic Disease Group (BIMDG) and the Royal College of Paediatrics and Child Health (RCPCH) have issued guidance on how clinically extremely vulnerable (CEV) adults and children will be assessed during lockdown...

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  5. 18.12.20

    NPUK News: Autumn/Winter 2020

    We are pleased to be able to share with you the latest issue of NPUK News. This Autumn/Winter 2020 issue is in fact the only physical magazine we have developed this year, due to issues presented by the COVID situation. We have instead provided monthly updates to keep our community as informed as possible during these strange times. An unintended positive is that this bumper 2020 edition serves as a reminder that despite the challenges this year has thrown at us as individuals, families, and as a community, we have much to be proud of and much to celebrate!

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