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  1. 26.07.19

    Survey Opportunity: Qualitative Analysis of Niemann-Pick Type C 5-Domain NPCCSS

    We are pleased to inform you of a study opportunity available to NPC patients and their families:
    Clinical Outcomes Solutions (COS), is a research company conducting research into Niemann-Pick type C (NPC) on behalf of a sponsor, Orphazyme A/S, a pharmaceutical company studying NPC...

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  2. 22.07.19

    Orphazyme to prepare for filing of arimoclomol in US for Niemann-Pick disease Type C (NPC)

    Following the encouraging regulatory agency feedback, Orphazyme plans to introduce an Early Access
    Program for NPC in the fall of 2019, to further accelerate access to treatment with arimoclomol for people
    living with NPC...

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  3. 18.07.19

    Anders Hinsby: Letter to NP-C Community

    Anders Hinsby: "I am writing to personally share the news that I will be resigning my position as Orphazyme’s Chief Executive Officer effective October 1, 2019..."

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  4. 15.07.19

    BOOK NOW: NPUK Interactive Workshop 2019

    This year the NPUK Interactive Workshop will take place on the 20th September at Wyboston Lakes, Bedfordshire - and will as ever be a fantastic opportunity for clinicians, health professionals and scientists working in the Niemann-Pick field to meet together under one roof...

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  5. 05.07.19

    BOOK NOW: NPUK Annual Family Conference 2019

    Our Annual Family Conference and Interactive Workshop on Niemann-Pick Diseases is the largest event in the NPUK calendar, bringing together affected individuals, families, health and research professionals under one roof...

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