07.11.18
The following letter from Mallinckrodt's Sheila Talafous, Director, Advocacy Relations and Derek Naten, Senior Director, Government Relations & Advocacy refers to the VTS-270 Phase 2b.3, as well as expanded access and compassionate use programs.
Read more04.10.18
CTD announces encouraging top-line data from two ongoing clinical trials of Trappsol® Cyclo™ administered intravenously in Niemann Pick Disease Type C (NPC)
Read more03.10.18
ORPHAZYME REPORTS ENCOURAGING ARIMOCLOMOL CLINICAL TRIAL TOP-LINE DATA IN NIEMANN-PICK DISEASE TYPE C (NPC)...
Read more13.09.18
The NPUK Annual Family Conference & Interactive Workshop is all set for next weekend, where you will once again get the opportunity to hear the latest developments regarding therapies and clinical trials for ASMD Niemann-Pick disease types A and B, and Niemann-Pick type C, plus related care issues, breakout sessions, and workshops...
Read more11.07.18
We are looking forward to this year's NPUK Annual Family Conference & Interactive Workshop on Niemann-Pick Diseases, which will mark a special milestone - the 25th time we are all coming together as a community!
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