05.10.17
The study was recently completed in May 2017. A total of 35 patients were enrolled across 12 sites in 8 countries. The primary objective of the 001 study was to characterize the individual patient’s disease progression profile through clinical, biological and quality-of-life measures recorded prospectively, as well as the historic disease information collected from patient medical records.
Read more20.09.17
There is an opportunity for you to participate in a market research study about Niemann-Pick Type C, conducted by an organization called ApotheCom on behalf of an industry sponsor. The goal of the study is to understand your preferences and concerns regarding the method through which a drug could be administered to manage Niemann-Pick Type C.
Read more20.09.17
We are pleased to inform you about an opportunity to share your story of living with Niemann-Pick Type C (NPC) in a market research study. An independent market research organisation, Magnolia Innovation, is currently conducting research with people, or parents of children, who have NP-C.
Read more18.09.17
The preliminary programme for this year's Annual Family Conference & Interactive Workshop is finally here - we are excited to once again welcome our community to the biggest event in the NPUK calendar!
Read more07.09.17
IntraBio announces plans for a multi-national randomised clinical trial to evaluate IB1000 as a therapeutic intervention for patients with NP-C...
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