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News

  1. 30.01.20

    Sanofi : Positive topline results demonstrated by olipudase alfa, first and only investigational therapy in late-stage development for acid sphingomyelinase deficiency

    Sanofi : Positive topline results demonstrated by olipudase alfa, first and only investigational therapy in late-stage development for acid sphingomyelinase deficiency...

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  2. 17.01.20

    IntraBio Completes NPC Clinical Trial Enrollment

    OXFORD, UK / ACCESSWIRE / January 17, 2020, / IntraBio Inc, a late-stage biopharmaceutical company, is pleased to share that it has completed enrollment for its IB1001-201 Clinical Trial...

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  3. 17.01.20

    IntraBio Neuroprotection and Disease Modification for Niemann-Pick C Extension Phase Approved in Europe

    OXFORD, UK / ACCESSWIRE / January 15, 2020 / IntraBio Inc., a late-stage biopharmaceutical company, is pleased to share that the Extension Phase for the IB1001-201 Clinical Trial has been approved in all European countries where the trial is being conducted...

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  4. 06.01.20

    Orphazyme Announcement: US Early Access Program for NPC

    Copenhagen, Denmark, January 6, 2020 – Orphazyme A/S (ORPHA.CO), a biopharmaceutical company pioneering Heat-Shock Protein response for the treatment of neurodegenerative orphan diseases, today announces the availability of an Early Access Program (EAP) in the United States (US) for its investigational drug arimoclomol for the treatment of Niemann-Pick disease Type C (NPC)...

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  5. 03.01.20

    Orphazyme reports positive arimoclomol data from open-label phase 2/3 extension in Niemann-Pick disease Type C

    • 12-month data from open-label extension trial show sustained effect in reducing disease progression over two years
    • New genetic sub-group analysis recommended by US Food and Drug Administration supports
    robustness of results
    • Filling of New Drug Application in US on track for H1 2020, with expected approval in H1 2021

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