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News

  1. 20.05.22

    CHMP recommends approval of Xenpozyme® (olipudase alfa), the first and only treatment for ASMD

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  2. 17.05.22

    Orphazyme A/S under In-Court-Restructuring to sell substantially all of its assets and business activities to KemPharm, Inc.

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  3. 27.04.22

    NPUK Care & Support Services Survey

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  4. 20.04.22

    Quality of life experience in patients with Niemann-Pick disease Type C during the COVID-19 pandemic research study

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  5. 28.03.22

    Xenpozyme® (olipudase alfa) approved in Japan, first and only approved therapy indicated to treat acid sphingomyelinase deficiency

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