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  1. 19.10.22

    Cyclo Therapeutics Announces Publication of Phase 1 Data for Trappsol® Cyclo™ for the Treatment of Niemann-Pick Disease Type C1 (NPC1)

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  2. 03.10.22

    301 NPC UK Recruitment Update - IntraBio

    IntraBio Ltd. is pleased to share that the Phase III pivotal trial with N-acetyl-L-leucine (IB1001-301) clinical trial has enrolled over 30% of the target number of patients in the first month of recruitment. The study, which investigates N-acetyl-L-leucine (IB1001) for the treatment of Niemann-Pick disease Type C (NPC), will enroll a total of approximately 52 patients across all international sites. Since recruitment commenced in September 2022, sixteen (20) patients have been screened...

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  3. 08.09.22

    Drug Repurposing for Rare Diseases 2022 is shifting its programme to match the new drug repurposing landscape.

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  4. 28.06.22

    Press Release: Xenpozyme® (olipudase alfa) approved by European Commission as first and only treatment for ASMD

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  5. 15.06.22

    IntraBio: IB1001-301 (UK Recruitment)

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