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News

  1. 07.11.18

    Mallinckrodt: VTS-270 Phase 2b.3 Data Announcement

    The following letter from Mallinckrodt's Sheila Talafous, Director, Advocacy Relations and Derek Naten, Senior Director, Government Relations & Advocacy refers to the VTS-270 Phase 2b.3, as well as expanded access and compassionate use programs.

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  2. 04.10.18

    CTD announces encouraging top-line data from two ongoing clinical trials of Trappsol® Cyclo™ administered intravenously in Niemann Pick Disease Type C (NPC)

    CTD announces encouraging top-line data from two ongoing clinical trials of Trappsol® Cyclo™ administered intravenously in Niemann Pick Disease Type C (NPC)

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  3. 03.10.18

    Orphazyme Reports Encouraging Arimoclomol Clinical Trial Top-line Data in Niemann-Pick Disease Type C (NP-C)

    ORPHAZYME REPORTS ENCOURAGING ARIMOCLOMOL CLINICAL TRIAL TOP-LINE DATA IN NIEMANN-PICK DISEASE TYPE C (NPC)...

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  4. 13.09.18

    NPUK Annual Family Conference & Interactive Workshop 2018 (Preliminary Programme)

    The NPUK Annual Family Conference & Interactive Workshop is all set for next weekend, where you will once again get the opportunity to hear the latest developments regarding therapies and clinical trials for ASMD Niemann-Pick disease types A and B, and Niemann-Pick type C, plus related care issues, breakout sessions, and workshops...

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  5. 11.07.18

    Are you looking forward to the NPUK Annual Family Conference?

    We are looking forward to this year's NPUK Annual Family Conference & Interactive Workshop on Niemann-Pick Diseases, which will mark a special milestone - the 25th time we are all coming together as a community!

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