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News

  1. 24.08.21

    Orphazyme announces publication of results from its Phase 2/3 trial of arimoclomol in Niemann-Pick disease type C in the Journal of Inherited Metabolic Disease

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  2. 19.08.21

    IntraBio Reports Statistically Significant and Clinically Meaningful Improvements in the Use of IB1001 For Treatment of GM2 Gangliosidosis (Tay-Sachs and Sandhoff disease)

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  3. 02.07.21

    NPUK are hiring! (Fundraising Officer)

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  4. 30.06.21

    Orphazyme presents 36-month data supporting durable response to arimoclomol during Parseghian Scientific Conference for NPC Research

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  5. 18.06.21

    Orphazyme: NPC Community Notification

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2023 Niemann-Pick UK (NPUK). Registered Charity: England and Wales (1144406) / Scotland (SCO45407). Registered as a company limited by guarantee in England and Wales (07775835).

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