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Genetic Disorders UK

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Genetic Disorder UK has a vision to improve the lives of individuals and families affected by genetic disorders. Genetic Disorders UK’s mission is to be the leading source of information and support for both those affected by a genetic disorder, and the charities and patient groups that support them, by bringing together everyone’s combined experience in a place it can be shared.

Rare Disease UK

rdukNPUK is a member of Rare Disease UK (RDUK). RDUK is the national alliance for people with rare diseases and all who support them. RDUK provides a united voice for the rare disease community by capturing the experiences of patients and families.

RDUK is working with health departments across the UK to implement the UK Strategy for Rare Diseases to ensure that patients and families living with rare conditions have equitable access to high quality services, treatment and support.

 

Genetic Alliance UK

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NPUK is a member of Genetic Alliance UK. Genetic Alliance UK aims to improve the lives of people affected by genetic conditions by ensuring that high quality services and information are available to all who need them. They are an alliance of over 180 patient organisations.

Together for Short Lives

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Together for Short Lives is the UK charity that speaks out for children and young people who are expected to have short lives. Together for Short Lives helps to provide these children and young people have as fulfilling lives as possible and the very best care at the end of life.

EURORDIS

eurordis-rvb-halfNPUK is a member of EURODIS. EURODIS is a non-governmental patient-driven alliance of patient organisations representing 716 rare disease patient organisations in 63 countries. It is the collective voice of over 30 million people affected by rare diseases throughout Europe.

The Specialised Healthcare Alliance

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The Specialised Healthcare Alliance (SHCA) is a coalition of patient-related groups and corporate supporters with a strong record of campaigning on behalf of people with rare and complex conditions in need of specialised care. These services cover a wide range of conditions, many of which could affect any one of us at some point in our lives.

Latest news

15.03.19

CTD Holdings Announces Plan to Launch Clinical Trial of Trappsol® Cyclo™ in Alzheimer’s Disease

ALACHUA, FL – (Globe Newswire) – March 14, 2019 – CTD Holdings, Inc. (OTCQB: CTDH), a clinical stage biotechnology company that develops cyclodextrin-based products for the treatment of disease with unmet medical need, announced today that the company has initiated planning for a Phase I clinical trial for treatment of Alzheimer’s Disease. The trial will use Trappsol® Cyclo™, the company’s proprietary formulation of hydroxypropyl beta cyclodextrin, administered intravenously.

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11.03.19

IntraBio Clinical Trial Authorization Application Approved by the MHRA for the Treatment of Niemann-Pick Disease type C (NPC)

IntraBio Clinical Trial Authorization Application Approved by the MHRA for the Treatment of Niemann-Pick Disease type C (NPC): OXFORD, UK, March 11, 2019-- IntraBio Inc., a late-stage biopharmaceutical company, today announced that the UK Medicines and Healthcare products Regulatory Agency (MHRA) has approved its Clinical Trial Authorisation (CTA) Application for Clinical Trial IB1001-201 with its lead compound (IB1001) for the treatment of Niemann-Pick disease Type C (NPC).

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