09.02.21
Data from ongoing Phase 1 extension study shows improvement in disease features or disease stabilization with home-based intravenous infusions of Trappsol® Cyclo™...
Read more05.02.21
Orphazyme to showcase data on arimoclomol in Niemann-Pick disease Type C during the 2021 Annual WORLDSymposium™...
Read more29.01.21
This webinar has been organised by patient organisations working in the field of Inherited Metabolic Diseases (IMD). We have realised from talking to IMD patients and families that there is some confusion about the COVID-19 vaccines...
Read more26.01.21
We are pleased to share the latest update from Cyclo Therapeutics entitled "Cyclo Therapeutics to Present on Its Clinical and Drug Development Program for Lead Candidate, Trappsol® Cyclo™, at WORLDSymposium 2021"...
Read more26.01.21
We are proud to have been nominated for the #EURORDISAwards2021 (EURORDIS Black Pearl Awards) this year, in the category of Visual and Audio Media Award...
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