News

Latest information for clinically extremely vulnerable adults and children

Both the British Inherited Metabolic Disease Group (BIMDG) and the Royal College of Paediatrics and Child Health (RCPCH) have issued guidance on how clinically extremely vulnerable (CEV) adults and children will be assessed during lockdown...

NPUK News: Autumn/Winter 2020

We are pleased to be able to share with you the latest issue of NPUK News. This Autumn/Winter 2020 issue is in fact the only physical magazine we have developed this year, due to issues presented by the COVID situation. We have instead provided monthly updates to keep our community as informed as possible during these strange times. An unintended positive is that this bumper 2020 edition serves as a reminder that despite the challenges this year has thrown at us as individuals, families, and as a community, we have much to be proud of and much to celebrate!

Cyclo Therapeutics Announces Pricing of $12.5 Million Public Offering

Cyclo Therapeutics Announces Two Presentations at WORLDSymposium2021

Orphazyme Submits European Marketing Authorisation Application for Arimocolmol for Treatment of Niemann-Pick disease type C