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News

  1. 24.02.22

    Orphazyme Announces Update on Regulatory Review of Arimoclomol in the European Union

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  2. 14.02.22

    IB1001-301: Effects of N-Acetyl-L-Leucine on Niemann-Pick disease type C (NPC): A Phase III, randomized, placebo-controlled, double-blind, crossover study

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  3. 11.02.22

    Orphazyme provides update for planned NDA resubmission for arimoclomol for the treatment of Niemann-Pick disease type C in the United States

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  4. 03.02.22

    Cyclo Therapeutics Announces Formation of Global Steering Committee Comprised of Leading Experts to Advise on the Global Phase 3 Clinical Development Program for Trappsol® Cyclo™ in Niemann-Pick Disease Type C

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  5. 01.02.22

    Changes to the Executive Management of Orphazyme – Anders Vadsholt to be appointed CEO

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2022 Niemann-Pick UK (NPUK). Registered Charity: England and Wales (1144406) / Scotland (SCO45407). Registered as a company limited by guarantee in England and Wales (07775835).

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