11.12.18
Orphazyme expects to announce results of full data set for Niemann-Pick disease Type C (NPC) Phase II/III trial in Q1 2019...
Read more30.11.18
16.11.18
We are happy to announce that the latest issue of NPUK News (Autumn 2018) is now available. This time around it is a bumper edition featuring everything from the Annual Family Conference to BBC Children in Need, with guest articles from Shona Beveridge, Jenny Charman, and Dave Smith...and so much more!
Read more07.11.18
The following letter from Mallinckrodt's Sheila Talafous, Director, Advocacy Relations and Derek Naten, Senior Director, Government Relations & Advocacy refers to the VTS-270 Phase 2b.3, as well as expanded access and compassionate use programs.
Read more04.10.18
CTD announces encouraging top-line data from two ongoing clinical trials of Trappsol® Cyclo™ administered intravenously in Niemann Pick Disease Type C (NPC)
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